{"id":6899,"date":"2026-06-05T20:26:23","date_gmt":"2026-06-05T20:26:23","guid":{"rendered":"https:\/\/medical.biomarin.com\/en-us\/?page_id=6899"},"modified":"2026-07-08T15:34:42","modified_gmt":"2026-07-08T15:34:42","slug":"bmn-333","status":"publish","type":"page","link":"https:\/\/medical.biomarin.com\/en-us\/bmn-333\/","title":{"rendered":"BMN 333"},"content":{"rendered":"<div id=\"acf-block-68de3cac2ef74\" class=\"hero hero-no-overlay hero-large-first-para\">\n            <div class=\"hero-background-image hero-background-image-desktop\" style=\"background-image: url(https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2025\/10\/Program-banner-bones.png?v=1.27);\"><\/div>\n\t    <div class=\"hero-background-image hero-background-image-mobile\" style=\"background-image: url(https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2025\/10\/Program-banner-bones-Mobile.png?v=1.27);\"><\/div>\n    \t<div class=\"overlay\"><\/div>\n\t<div class=\"wrapper\">\n\t\t<div class=\"inner-wrapper\">\n\t\t\t<div class=\"hero-content\">\n\t\t\t    \t\t\t\t\t\t\t\t\t\t\t\t    <h1>BMN 333\n<\/h1>\n\t\t\t\t\t\t\t\t\t\t\t\t    <p>Learn more about BioMarin research in Long-Acting CNP<\/p>\n\t\t\t\t\t\t\t\t\n                <p class=\"inline-buttons\">\n                                                        <\/p>\n\t\t\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t<\/div>\n<\/div>\n\n\n<div id=\"acf-block-68e7d6279a7e3\" class=\"block cards cards-2-col\">\n\t<div class=\"wrapper\">\n\t\t<div class=\"inner-wrapper\">\n\t\t\t<div class=\"cards-title\">\n\t\t\t    \t\t\t\t\t\t\t<\/div>\n\t\t\t<div class=\"cards-wrapper\">\n\t\t\t    \n<div id=\"acf-block-68e7d6279ad98\" class=\"card card-product card-fixed-button\" data-muted-autoplay=\"false\">\n        <div class=\"card-content\">\n                            <h4>Clinical Program\n<\/h4>\n        \n                                                                                                                                                                                                                                                                                    \n                                                                                        <\/div>\n                                <div class=\"card-actions\">\n                            \n                            <p><a class=\"button button-arrow\" href=\"#acf-block-68e7d627a167c\" target=\"_self\">See clinical trials<\/a><\/p>\n                                                                                    <\/div>\n<\/div>\n\n<div id=\"acf-block-68e7d6279ae37\" class=\"card card-product card-fixed-button\" data-muted-autoplay=\"false\">\n        <div class=\"card-content\">\n                            <h4>Congress Posters and Presentations\n<\/h4>\n        \n                                                                                                                                                                                                                                                                                    \n                                                                                        <\/div>\n                                <div class=\"card-actions\">\n                            \n                            <p><a class=\"button button-arrow\" href=\"#acf-block-68ecfd62c135f\" target=\"_self\">See posters &amp; presentations<\/a><\/p>\n                                                                                    <\/div>\n<\/div>\n\t\t\t<\/div>\n\t\t<\/div>\n\t<\/div>\n<\/div>\n\n<div id=\"acf-block-68e7d627a167c\" class=\"vblock pipeline pipeline-listing-wrapper no-pipeline-filters\">\n\t<!-- Pipeline Filter Header\n\tIntegration notes:\n\t- Toggle button-filter-active class to filter button when active\n\t- Component here is generic filter header and is also used for resources (filters themselves differ)\n\t-->\n\t<div class=\"block filter-header\">\n\t\t<div class=\"wrapper\">\n\t\t\t<div class=\"inner-wrapper\">\n\t\t\t\t<h1>BMN 333 Long-Acting CNP Research<\/h1>\n\t\t\t\t\n\t\t\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t<\/div>\n\n\t<!-- Research Pipeline block -->\n\t<div class=\"block bg-band pipeline-listing-main\">\n\t\t<div class=\"wrapper\">\n\t\t\t<div class=\"inner-wrapper\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t                    \n\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-listing pipeline-skeletal-conditions\">\n\t\t\t\t\t\t<h2 class=\"h3\">Skeletal Conditions<\/h2>\n\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h3 class=\"h5 trial-phase trial-phase\">Trial phase<\/h3>\n\n\t\t\t\t\t\t\t<div class=\"pipeline-group\" data-trial-phase-class=\"trial-phase\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-headers\">\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-headers-summary\">\n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-product\">Program (Trial)<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-condition\">Condition<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-phase\">Phase<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<\/div>\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t<article class=\"pipeline-trial filter-condition-achondroplasia filter-tech-peptide filter-rec-stat-recruiting phase-3\">\n\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-summary\">\n\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-headers-summary\">\n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-product\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t<h3 class=\"h5\">BMN 333 Long-Acting CNP<\/h3>\n\t\t\t\t\t\t\t\t\t\t\t\t\t<p>(333-301 [ASPEN])<\/p>\n\t\t\t\t\t\t\t\t\t\t\t\t\t<p class=\"status\"><span class=\"label\">Trial Status<\/span> <span class=\"status\">Recruiting<\/span><\/p>\n\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-condition\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4 class=\"h5\">Condition<\/h4>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t<p>Achondroplasia<\/p>\n\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-phase\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4 class=\"h5\">Phase<\/h4>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t<ul>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<li>Phase 3<\/li>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/ul>\n\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-details\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4>Title<\/h4>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t<p>A Phase 2\/&#x200B;3 Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia (ASPEN)<\/p>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4>Study Description<\/h4>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t<p>To evaluate the effects of BMN 333 on growth compared with vosoritide in participants with achondroplasia who have not received any growth-promoting treatments. The study includes 2 parts: the Phase 2 part will select the optimal BMN 333 dose to be used in Phase 3 and determine study continuation into Phase 3; the Phase 3 part will compare the effects of the selected dose of BMN 333 with vosoritide.<\/p>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"detail-boxes\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"box\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4>Primary Outcome Measure*<\/h4>\n<ul>\n<li>Predicted annualized growth velocity (AGV; Phase 2) and AGV (Phase 3)<\/li>\n<\/ul>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"box\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4>Select Inclusion Criteria*<\/h4>\n<ul>\n<li>Aged &ge; 2 to &lt; 11 years (Phase 2) or &ge; 2 to &lt; 18 years (Phase 3)<\/li>\n<li>Achondroplasia (confirmed by documented genetic testing) and open epiphyses<\/li>\n<li>Tanner Stage I (Phase 2) or any Tanner stage (Phase 3)<\/li>\n<li>Ambulatory and able to stand without assistance<\/li>\n<\/ul>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"box\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4>Secondary Outcome Measures*<\/h4>\n<ul>\n<li>Change from baseline in standing height, height Z-score, and upper to lower body segment ratio<\/li>\n<li>Incidence of adverse events (AEs), serious AEs, and events of interest<\/li>\n<\/ul>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"box\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<h4>Select Exclusion Criteria*<\/h4>\n<ul>\n<li>Any short stature condition other than achondroplasia<\/li>\n<li>History of any renal insufficiency or cardiac\/ cardiovascular disease that places the participant at increased risk of an adverse cardiac outcome in the setting of hypotension<\/li>\n<li>Bone fractures of the long bones or spine within 6 months prior to screening<\/li>\n<li>Used vosoritide, any other approved product (except growth hormone [GH], as detailed below), investigational product, or investigational medical device for the treatment of achondroplasia or short stature at any time<\/li>\n<li>Been treated with GH, insulin-like growth factor 1, or anabolic steroids in the 6 months prior to treatment start<\/li>\n<\/ul>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\n\t\t\t\t\t\t\t\t\t\t\t\t\t<p>* Additional measures\/criteria may apply.<\/p>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<p><a class=\"button button-text button-external\" href=\"https:\/\/clinicaltrials.gov\/study\/NCT07441876\" target=\"_blank\">For reference and comprehensive trial information, visit ClinicalTrials.gov NCT07441876<\/a><\/p>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<\/div>                                            \n\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-action\">                                                \n\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"pipeline-expand\">\n\t\t\t\t\t\t\t\t\t\t\t\t\t<div class=\"trigger\"><\/div>\n\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t<\/article>\n\t\t\t\t\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t\t\t\t\t<\/div>\n\t\t\t\t\t\t\t<\/div>\n\t\t<\/div>\n\t<\/div>\n<\/div>\n\n<div id=\"acf-block-68ecfd62c135f\" class=\"block resources-listing\">\n\t<div class=\"wrapper\">\n\t\t<div class=\"inner-wrapper\">\n\n                            <div class=\"listing-title\">\n                                            <h2>Congress Posters and Presentations\n<\/h2>\n                                                                <p>All displayed posters and presentations are protected by copyright and are intended for individual use only.<\/p>\n<p><i><b>Please Note<\/b>: Poster content may be unavailable or delayed. This could be due to copyright or embargo guidelines.<\/i><\/p>\n<p>You may check back later or contact&#xA0;<a href=\"mailto:medinfo@bmrn.com\">medinfo@bmrn.com<\/a>&#xA0;or&#xA0;<a class=\"external_link\" href=\"https:\/\/www.biomarin.com\/web-request-form?_gl=1*1hs6n10*_ga*MTg0MDExMDAwMS4xNjg2MDQ0Nzc4*_ga_KGGE14VN95*MTY4NjEzNTY1Ni4xMC4xLjE2ODYxMzU3OTAuMC4wLjA.&amp;_ga=2.9066165.141314881.1686044782-1840110001.1686044778\" target=\"_blank\" rel=\"noopener\">complete a request form<\/a>&#xA0;to inquire about this specific material<\/p>\n                                    <\/div>\n\t\t\t\t\t\t                                    \n                    \n                                                                                                                                                                                                                                                                                                                                \n                                                                                        \n                                        <article class=\"resource resource-poster\">\n                                                    <p class=\"resource-type\">Poster<\/p>\n                                                <div class=\"resource-split-layout\">\n                            <div class=\"resource-image-block\">\n                                <div class=\"resource-image\">\n                                                                            <div class=\"resource-feature-image\" style=\"background-image: url(https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2025\/05\/Congresses-1-1024x576.png);\"><\/div>\n                                                                    <\/div>\n                                                                                                                                                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ICCBH-2026_BMN_333_Development_poster_P158_MED-SC-0712.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ICCBH\" data-product=\"2026\">View content<\/a><\/p>\n                                                                                            <\/div>\n                            <div class=\"resource-information\">\n                                                                    <p class=\"new-flag\">New<\/p>\n                                                                                                    <div class=\"resource-meta\">\n                                                                                    <ul class=\"tags\">\n                                                                                                    <li>Congresses<\/li>\n                                                                                                    <li>BMN 333 Long-Acting CNP Research<\/li>\n                                                                                                    <li>Achondroplasia<\/li>\n                                                                                                    <li>ICCBH<\/li>\n                                                                                                    <li>2026<\/li>\n                                                                                            <\/ul>\n                                                                                                                    <\/div>\n                                                                                                                                    <h2>Development of BMN 333, a long-acting version of vosoritide for FGFR3-related dwarfism and other skeletal dysplasias\n<\/h2>\n                                                                                                <div class=\"resource-links\">\n                                                                                                                                                            \t                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ICCBH-2026_BMN_333_Development_poster_P158_MED-SC-0712.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ICCBH\" data-product=\"2026\">View content<\/a><\/p>\n                                                                    <\/div>\n                                                            <\/div>\n                        <\/div>\n                    <\/article>\n                                    \n                    \n                                                                                                                                                                                                                                                                                                                                \n                                                                                        \n                                        <article class=\"resource resource-poster\">\n                                                    <p class=\"resource-type\">Poster<\/p>\n                                                <div class=\"resource-split-layout\">\n                            <div class=\"resource-image-block\">\n                                <div class=\"resource-image\">\n                                                                            <div class=\"resource-feature-image\" style=\"background-image: url(https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2025\/05\/Congresses-1-1024x576.png);\"><\/div>\n                                                                    <\/div>\n                                                                                                                                                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ICCBH-2026_BMN_333_Bone_Growth_NHPs_P79_MED-SC-0712.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ICCBH\" data-product=\"2026\">View content<\/a><\/p>\n                                                                                            <\/div>\n                            <div class=\"resource-information\">\n                                                                    <p class=\"new-flag\">New<\/p>\n                                                                                                    <div class=\"resource-meta\">\n                                                                                    <ul class=\"tags\">\n                                                                                                    <li>Congresses<\/li>\n                                                                                                    <li>BMN 333 Long-Acting CNP Research<\/li>\n                                                                                                    <li>Achondroplasia<\/li>\n                                                                                                    <li>ICCBH<\/li>\n                                                                                                    <li>2026<\/li>\n                                                                                            <\/ul>\n                                                                                                                    <\/div>\n                                                                                                                                    <h2>Endochondral bone growth with weekly BMN 333, a long-acting vosoritide investigational product, in juvenile nonhuman primates\n<\/h2>\n                                                                                                <div class=\"resource-links\">\n                                                                                                                                                            \t                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ICCBH-2026_BMN_333_Bone_Growth_NHPs_P79_MED-SC-0712.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ICCBH\" data-product=\"2026\">View content<\/a><\/p>\n                                                                    <\/div>\n                                                            <\/div>\n                        <\/div>\n                    <\/article>\n                                    \n                    \n                                                                                                                                                                                                                                                                                                                                \n                                                                                        \n                                        <article class=\"resource resource-poster\">\n                                                    <p class=\"resource-type\">Poster<\/p>\n                                                <div class=\"resource-split-layout\">\n                            <div class=\"resource-image-block\">\n                                <div class=\"resource-image\">\n                                                                            <div class=\"resource-feature-image\" style=\"background-image: url(https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2025\/05\/Congresses-1-1024x576.png);\"><\/div>\n                                                                    <\/div>\n                                                                                                                                                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ICCBH-2026_333_Study_Design_poster_P84_MED-SC-0712.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ICCBH\" data-product=\"2026\">View content<\/a><\/p>\n                                                                                            <\/div>\n                            <div class=\"resource-information\">\n                                                                    <p class=\"new-flag\">New<\/p>\n                                                                                                    <div class=\"resource-meta\">\n                                                                                    <ul class=\"tags\">\n                                                                                                    <li>Congresses<\/li>\n                                                                                                    <li>BMN 333 Long-Acting CNP Research<\/li>\n                                                                                                    <li>Achondroplasia<\/li>\n                                                                                                    <li>ICCBH<\/li>\n                                                                                                    <li>2026<\/li>\n                                                                                            <\/ul>\n                                                                                                                    <\/div>\n                                                                                                                                    <h2>BMN 333 clinical development program in achondroplasia: Phase 1 results and phase 2\/3 study design overview\n<\/h2>\n                                                                                                <div class=\"resource-links\">\n                                                                                                                                                            \t                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ICCBH-2026_333_Study_Design_poster_P84_MED-SC-0712.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ICCBH\" data-product=\"2026\">View content<\/a><\/p>\n                                                                    <\/div>\n                                                            <\/div>\n                        <\/div>\n                    <\/article>\n                                    \n                    \n                                                                                                                                                                                                                                                                                                                                \n                                                                                        \n                                        <article class=\"resource resource-poster\">\n                                                    <p class=\"resource-type\">Poster<\/p>\n                                                <div class=\"resource-split-layout\">\n                            <div class=\"resource-image-block\">\n                                <div class=\"resource-image\">\n                                                                            <div class=\"resource-feature-image\" style=\"background-image: url(https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2025\/05\/Congresses-1-1024x576.png);\"><\/div>\n                                                                    <\/div>\n                                                                                                                                                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ENDO-2026_333_PK-PD-poster_MED-SC-0687.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ENDO\" data-product=\"2026\">View content<\/a><\/p>\n                                                                                            <\/div>\n                            <div class=\"resource-information\">\n                                                                    <p class=\"new-flag\">New<\/p>\n                                                                                                    <div class=\"resource-meta\">\n                                                                                    <ul class=\"tags\">\n                                                                                                    <li>Congresses<\/li>\n                                                                                                    <li>BMN 333 Long-Acting CNP Research<\/li>\n                                                                                                    <li>Achondroplasia<\/li>\n                                                                                                    <li>ENDO<\/li>\n                                                                                                    <li>2026<\/li>\n                                                                                            <\/ul>\n                                                                                                                    <\/div>\n                                                                                                                                    <h2>BMN&#x202F;333 Achieves High Sustained Released Vosoritide Exposure with Favorable Safety: Phase&#x202F;1 Results that Support Phase&#x202F;2\/3 Trials in Achondroplasia\n<\/h2>\n                                                                                                <div class=\"resource-links\">\n                                                                                                                                                            \t                                                                                                                                                                        <p><a class=\"button modal-pdfjs permitted\" href=\"https:\/\/medical.biomarin.com\/en-us\/wp-content\/uploads\/sites\/2\/2026\/06\/ENDO-2026_333_PK-PD-poster_MED-SC-0687.pdf?v=1.27\" target=\"_blank\" data-format=\"Poster\" data-topic=\"Congresses\" data-audience=\"BMN 333 Long-Acting CNP Research\" data-disease-state=\"Achondroplasia\" data-region=\"ENDO\" data-product=\"2026\">View content<\/a><\/p>\n                                                                    <\/div>\n                                                            <\/div>\n                        <\/div>\n                    <\/article>\n                            \t\t<\/div>\n\t<\/div>\n<\/div>","protected":false},"excerpt":{"rendered":"","protected":false},"author":3,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"inline_featured_image":false,"footnotes":""},"class_list":["post-6899","page","type-page","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v28.1 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>BMN 333 | BioMarin Medical<\/title>\n<meta name=\"description\" content=\"Learn more about Duchenne muscular dystrophy (DMD) and BioMarin research\" \/>\n<meta name=\"robots\" content=\"index, follow, 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