Presentation
Efficacy and safety of valoctocogene roxaparvovec for severe hemophilia A 5 years after gene transfer in GENEr8-1
Presenting Author: Johnny Mahlangu
A. D. Leavitt, P. Raheja, E. Symington, D. V. Quon, A. Giermasz, G. Kenet, G. Lowe, N. S. Key, C. M. Millar, S. W. Pipe, S. Chou, R. Klamroth, J. Mason, H. Chambost, F. Peyvandi, E. Majerus, D. Pepperell, K. M. Chavele, M. C. Ozelo