This website is intended only for US healthcare professionals; if you are not a US healthcare professional, please visit www.BioMarin.com

BioMarin Medical

An online medical resource for healthcare providers in the United States to learn about BioMarin therapies and associated scientific and clinical information.

Disease States and Programs

Learn more about select therapeutic areas for which BioMarin has a therapy, either in development or approved by the FDA.

Bone

Achondroplasia

Learn more about achondroplasia and BioMarin therapies

Learn more

Access Achondroplasia Congress Posters and Presentations

Blood

Hemophilia A

Learn more about Hemophilia A and BioMarin therapies

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Access Hemophilia Congress Posters and Presentations

Brain

Phenylketonuria (PKU)

Learn more about PKU and BioMarin therapies

Learn more

Access PKU Congress Posters and Presentations

Mucopolysaccharidosis (MPS)

Learn more about MPS and BioMarin therapies

Mucopolysaccharidosis (MPS)

Mucopolysaccharidosis (MPS) Congress Posters and Presentations

Neuronal Ceroid Lipofuscinosis type 2 (CLN2)

Learn more about CLN2 Disease and BioMarin therapies

Neuronal Ceroid Lipofuscinosis type 2 (CLN2)

Neuronal Ceroid Lipofuscinosis type 2 (CLN2) Congress Posters and Presentations