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Publications

Learn more about mucopolysaccharidosis and BioMarin therapies

Mucopolysaccharidosis Publications List:

Publication

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  • Publications
  • MPS IVA
  • Real World Evidence
  • Safety and Efficacy Profile

Long-term outcomes of elosulfase alfa enzyme replacement therapy in adults with MPS IVA: a sub-analysis of the Morquio A Registry Study (MARS)

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Publication

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  • Publications
  • MPS VI
  • Safety and Efficacy Profile

Long-term enzyme replacement therapy: Findings from the mucopolysaccharidosis VI clinical surveillance program after 15 years follow-up

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Selected Publications

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  • Publications
  • MPS VI

Access selected publications on MPS VI and galsufase therapy.

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Selected Publications

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  • Publications
  • MPS IVA

Access selected publications on MPS IVA and its diagnosis and elosulfase alfa therapy.

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